N-Lorem Foundation

N-Lorem Foundation Creating a better future for nano-rare, one patient at a time.

Delivering individualized A*O medicines to more nano-rare patients requires continual innovation in how therapies are di...
08/31/2026

Delivering individualized A*O medicines to more nano-rare patients requires continual innovation in how therapies are discovered, developed, and advanced to the clinic. In this presentation, Dr. Julie Douville will describe how n-Lorem has built an efficient and flexible preclinical development model that accelerates programs while maintaining the highest standards of scientific quality.

Register for this event at no cost: https://www.nlorem.org/nano-rare-patient-colloquium-2026/

Ensuring a timely, consistent, objective, and scientifically rigorous evaluation of each patient has always been fundame...
08/28/2026

Ensuring a timely, consistent, objective, and scientifically rigorous evaluation of each patient has always been fundamental to n-Lorem's mission. In this presentation, Megan Knutsen will describe how n-Lorem is continually enhancing the efficiency of its patient review and physician onboarding processes while maintaining its commitment to thoughtful and objective patient selection. We will discuss improvements in patient intake, multidisciplinary review, and decision-making that streamline evaluation and reduce the time required to determine whether an individualized A*O strategy is appropriate. The session will also highlight key lessons learned which have increased clinical operations efficiency and created an improved experience for both physicians and patients.

Learn more about this free event: https://www.nlorem.org/nano-rare-patient-colloquium-2026/

The Rescue 7 Colloquium Family Club is returning to the 2026 Nano-rare Patient Colloquium! Founded by n-Lorem families w...
08/28/2026

The Rescue 7 Colloquium Family Club is returning to the 2026 Nano-rare Patient Colloquium! Founded by n-Lorem families who are first responders and veterans, Rescue 7 provides a family-friendly space featuring fun, firefighting-themed activities near the main Colloquium room, giving parents and children a place to relax, decompress, and take breaks throughout the event. Please note that the Family Club is not a drop-off space, and a parent or guardian should remain with their children while using the space. Gear up for some family fun!

Questions? Contact: [email protected]

As n-Lorem's treated patient population continues to grow, so does our understanding of the potential impact of individu...
08/27/2026

As n-Lorem's treated patient population continues to grow, so does our understanding of the potential impact of individualized A*O medicines across a broad range of nano-rare diseases. In this presentation, Dr. Laurence Mignon will provide an overview of the aggregate clinical experience across the n-Lorem patient community. By examining the collective experience, we will highlight the common themes emerging across programs, the lessons learned from treating an expanding patient population, and how these findings continue to strengthen our understanding of individualized A*O medicines and their potential to improve the lives of nano-rare patients.

Free registration: https://www.nlorem.org/nano-rare-patient-colloquium-2026/

We're excited to welcome Synoligo Biotechnologies to our superb list of Nano-rare Patient Colloquium 2026 sponsors!Synol...
08/27/2026

We're excited to welcome Synoligo Biotechnologies to our superb list of Nano-rare Patient Colloquium 2026 sponsors!

Synoligo enables many scientific discoveries through high-quality oligonucleotide synthesis and screening. Thank you, Synoligo, for your support of the Colloquium and nano-rare patients! đź‘Ź We look forward to an exciting event!

đź”—: https://www.nlorem.org/nano-rare-patient-colloquium-2026/

08/26/2026

Sally Jackson is a former actress, cookbook co-author, and mother of Susannah. In this Realities of the Nano-rare episode, Sally lets us into her family’s bubble, speaking candidly about the deeply complex and often terrifying realities of navigating KIF1A-associated neurological disorder. From helping Susannah's sibling understand the harsh consequences of her disease to confronting distress, uncertainty, and the profound unfairness of it all, Sally shares the difficult truths her family has faced and continues to carry and fight through.

Watch: https://youtu.be/PK1nxTywSEI

08/20/2026

We’re nearly 45 days away from the biggest n-Lorem community event of the year!

Join us October 7–8 for the 2026 Nano-rare Patient Colloquium, two days dedicated to connection, shared learning, meaningful conversations, and celebrating the progress of our nano-rare community.

Whether you join us in Cambridge or virtually, we hope to see you there. Register for free at nlorem.org.

As n-Lorem continues to demonstrate that individualized A*O medicines can safely deliver meaningful benefit, demand from...
08/19/2026

As n-Lorem continues to demonstrate that individualized A*O medicines can safely deliver meaningful benefit, demand from the nano-rare community has grown rapidly. In this presentation, Amy Williford will review the trajectory of patient demand for access to n-Lorem, the factors driving that growth, and the practical upper limits of the organization’s capacity today. The presentation will also explore how the n-Lorem model becomes more efficient and informative when a single A*O can treat multiple patients.

We hope that you'll join us for the ! Register: https://www.nlorem.org/nano-rare-patient-colloquium-2026/

Inherited retinal diseases are an important cause of progressive vision loss and blindness, yet patients with nano-rare ...
08/18/2026

Inherited retinal diseases are an important cause of progressive vision loss and blindness, yet patients with nano-rare genetic eye disease have few therapeutic options. In this presentation, Dr. Shyamanga Borooah will first broadly describe the current landscape of inherited retinal disease and its treatment. He will then focus on the early findings from year 1 of a first-in-human trial targeting a mutation in the inherited retinal disease gene PRPH2. This presentation highlights the potential of individualized A*Os to preserve vision by targeting the underlying genetic cause of disease and demonstrates how n-Lorem’s platform can move beyond neurological disease to potentially impact many patients with sight threatening genetic eye disease.

Register to attend the in-person or virtually at no cost: https://www.nlorem.org/nano-rare-patient-colloquium-2026/

Exceptional patient safety begins long before an A*O reaches the clinic. In this presentation, we will demonstrate how...
08/14/2026

Exceptional patient safety begins long before an A*O reaches the clinic. In this presentation, we will demonstrate how n-Lorem's rigorous preclinical development process is designed to identify, understand, and mitigate potential risks before treatment begins.

Free virtual or in-person registration: https://www.nlorem.org/2026-nrpc-registration/

Address

Carlsbad, CA

Website

Alerts

Be the first to know and let us send you an email when N-Lorem Foundation posts news and promotions. Your email address will not be used for any other purpose, and you can unsubscribe at any time.

Shortcuts

Share

Category