Cure SPG50

Cure SPG50 To help children affected by the SPG50 disease

What amazing and exciting news for our SPG50 community!
02/04/2026

What amazing and exciting news for our SPG50 community!

New SPG50 Gene Therapy Trial
Interventional / Gene Therapy Study

This clinical trial is enrolling participants in an interventional (gene therapy) study for individuals with SPG50. Enrollment into the treated arm is limited, protocol-defined, and site-specific.

How it works
📋 1 gene therapy treatment delivered by a single spinal procedure
📋 Follow-up visits to monitor health and development over time

Important information
🔹 Treated-arm enrollment is limited
🔹 Eligibility is determined by the clinical trial protocol
🔹 Additional study sites in Italy and Spain are enrolling soon

📩 Email Please contact [email protected] for questions about trial status and eligibility. More details can be found here https://lnkd.in/gS9g2ssQ

🔗 Register with Citizen Health to receive updates about future studies and https://lnkd.in/gyVaGCQq

Dear AP4 community,CureSPG50 has partnered with Citizen Health!! We're calling on all the AP4s community to sign up to C...
07/30/2025

Dear AP4 community,

CureSPG50 has partnered with Citizen Health!!

We're calling on all the AP4s community to sign up to Citizen Health today!

https://www.citizen.health/partners/curespg50

Citizen Health is an incredible (and FREE!) platform that helps you keep all your child’s health records in one place and track your child’s data secure, organized, and always accessible. This includes appointments, therapies, or studies your child has been part of, Citizen makes it easier to manage everything in one spot and you can access the data free of charge.

Why is this important? Because it helps us:
Know who you are…
Keep you in the loop when new studies are launched and potentially include you in our upcoming trials..

This is your chance to contribute directly to research while also benefiting from tools that support your own health journey.

Spread the word… the more AP4s who sign up, the stronger our data and the better our studies!

CureSPG50 has partnered with Citizen Health to help patients and families use their health data to improve care and drive groundbreaking treatments.

Address

Toronto, ON

Telephone

+14168292223

Website

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